A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

Study Identifier:
CLI-06657AA1-01
ClinicalTrials.gov Identifier:
EudraCT Identifier:
N/A
Study Contact Information:
Recruiting

Study Details

Medical Condition
  • Fabry Disease
Study Drug
  • Drug: PRX-102 1 mg/kg every two weeks
Date
Feb 2025 - Dec 2027
Patient Requirements
Sex: Female & Male
Age: 2 - 17 Years
Requirements Information
Healthy Volunteers
No

Protocol Summary

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents with Fabry Disease.

Study Locations

Location
Status
Location
Phoenix Children's
Phoenix, Arizona, United States, 85016
Status
Not yet recruiting
Location
Emory Genetics Clinical Trials Center
Atlanta, Georgia, United States, 30322
Status
Not yet recruiting
Location
University of Iowa
Iowa City, Iowa, United States, 52242
Status
Not yet recruiting
Location
Vivo Infusion
Grand Rapids, Michigan, United States, 49525
Status
Not yet recruiting
Location
Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, United States, 45229
Status
Not yet recruiting
Location
University of Utah
Salt Lake City, Utah, United States, 84108
Status
Not yet recruiting